Linkage to chromosome 2q36.1 in autosomal dominant Dandy-Walker malformation with occipital cephalocele and evidence for genetic heterogeneity

Hum Genet. 2008 Apr;123(3):237-45. doi: 10.1007/s00439-008-0467-y. Epub 2008 Jan 19.

Abstract

We previously reported a Vietnamese-American family with isolated autosomal dominant occipital cephalocele. Upon further neuroimaging studies, we have recharacterized this condition as autosomal dominant Dandy-Walker with occipital cephalocele (ADDWOC). A similar ADDWOC family from Brazil was also recently described. To determine the genetic etiology of ADDWOC, we performed genome-wide linkage analysis on members of the Vietnamese-American and Brazilian pedigrees. Linkage analysis of the Vietnamese-American family identified the ADDWOC causative locus on chromosome 2q36.1 with a multipoint parametric LOD score of 3.3, while haplotype analysis refined the locus to 1.1 Mb. Sequencing of the five known genes in this locus did not identify any protein-altering mutations. However, a terminal deletion of chromosome 2 in a patient with an isolated case of Dandy-Walker malformation also encompassed the 2q36.1 chromosomal region. The Brazilian pedigree did not show linkage to this 2q36.1 region. Taken together, these results demonstrate a locus for ADDWOC on 2q36.1 and also suggest locus heterogeneity for ADDWOC.

Publication types

  • Case Reports
  • Comparative Study
  • Research Support, N.I.H., Extramural

MeSH terms

  • Child, Preschool
  • Chromosome Deletion
  • Chromosomes, Human, Pair 2 / genetics*
  • Dandy-Walker Syndrome / complications
  • Dandy-Walker Syndrome / genetics*
  • Encephalocele / complications
  • Encephalocele / genetics*
  • Female
  • Genes, Dominant
  • Genetic Heterogeneity*
  • Genetic Linkage / genetics*
  • Genome, Human
  • Genotype
  • Humans
  • In Situ Hybridization, Fluorescence
  • Male
  • Nucleic Acid Hybridization
  • Occipital Bone / abnormalities*
  • Pedigree
  • Polymorphism, Single Nucleotide / genetics*