Abstract
Episodic ataxia type 2 (EA2) is an autosomal dominant channelopathy characterized by paroxysmal cerebellar ataxia. Previous studies suggest that most EA2 cases are associated with mutations in the alpha1A subunit of the P/Q-type voltage-gated calcium channel gene CACNA1A. In a UK national study, the authors analyzed 15 index cases with typical EA2 and identified two unreported intronic mutations that predict aberrant splicing.
Publication types
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Research Support, N.I.H., Extramural
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Research Support, Non-U.S. Gov't
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Research Support, U.S. Gov't, P.H.S.
MeSH terms
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Adolescent
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Adult
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Alternative Splicing / genetics*
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Calcium Channels / genetics*
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Cerebellar Ataxia / genetics*
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Cerebellar Ataxia / metabolism
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Cerebellar Ataxia / physiopathology
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Child
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Child, Preschool
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Chromosome Mapping
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Chromosomes, Human, Pair 19 / genetics
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DNA Mutational Analysis
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Female
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Genes, Dominant
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Genetic Markers / genetics
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Genetic Predisposition to Disease / genetics
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Genetic Testing
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Humans
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Infant
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Introns / genetics
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Male
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Mutation / genetics*
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Pedigree
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Polymorphism, Genetic / genetics
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Protein Subunits / genetics
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RNA / genetics*
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RNA Splice Sites / genetics
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United Kingdom
Substances
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CACNA1A protein, human
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Calcium Channels
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Genetic Markers
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Protein Subunits
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RNA Splice Sites
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RNA