A novel insertion mutation in spastin gene is the cause of spastic paraplegia in a Chinese family

J Neurol Sci. 2003 Jun 15;210(1-2):35-9. doi: 10.1016/s0022-510x(03)00011-x.

Abstract

A total of eight loci for autosomal dominant hereditary spastic paraplegia (ADHSP) has been mapped to chromosome 14q, 2p, 15q, 8q, 10q, 12q, 19q, 2q, respectively, among which the SPG4 gene on chromosome 2p21-22 encoding spastin, an ATPase of the AAA family, accounts for 40-50% of all ADHSP families and is expressed in both adult and fetal tissues. In this work, we reveal a novel insertion mutation in exon 11 of the SPG4 gene found in a big Chinese family composed of 47 members, including 20 affected ones, using linkage analysis. The mutation was well demonstrated to be the cause of loss of production of the functional protein by pre-termination of translation in AAA cassette region. To our knowledge, this is the first report of spastin mutation in China.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenosine Triphosphatases
  • Asian People / genetics*
  • Calcium-Binding Proteins / genetics*
  • DNA Mutational Analysis / methods
  • Exons
  • Family Health
  • Female
  • Genes, Dominant
  • Genetic Linkage
  • Genotype
  • Humans
  • Male
  • Molecular Sequence Data
  • Mutagenesis, Insertional*
  • Phenotype
  • Restriction Mapping
  • Spastic Paraplegia, Hereditary / etiology
  • Spastic Paraplegia, Hereditary / genetics*
  • Spastin

Substances

  • Calcium-Binding Proteins
  • Adenosine Triphosphatases
  • Spastin
  • SPAST protein, human