CD28 costimulation and immunoaffinity-based selection efficiently generate primary gene-modified T cells for adoptive immunotherapy

Blood. 2003 Jan 15;101(2):476-84. doi: 10.1182/blood-2002-07-2142. Epub 2002 Aug 22.

Abstract

The introduction of an inducible suicide gene has been proposed as a strategy to exploit the antitumor reactivity of donor T cells after allogeneic hematopoietic stem cell transplantation but permit control of graft-versus-host disease. However, there are several obstacles to this approach that may impair the ability of T cells to function and survive in vivo. These include the requirement for in vitro activation or long-term culture to introduce the transgene and obtain therapeutic cell numbers, the toxicity of drug selection to enrich transduced cells, and the immunogenicity of the transgene-encoded products. Here we have developed a transduction and selection strategy for generating large numbers of polyclonal T cells transduced with a retroviral vector encoding the human low-affinity nerve growth factor receptor (LNGFR) for selection and a Fas-based suicide construct (LV'VFas). Ligation of CD28 in conjunction with a T-cell receptor signal permitted efficient transduction, substantially promoted T-cell growth, and contributed to the generation of gene-modified T cells that retained clonal diversity, functional properties, and a homing receptor profile similar to untransduced peripheral blood lymphocytes. Microbeads conjugated directly to antibody specific to LNGFR significantly improved the immunomagnetic selection of LV'VFas-modified T cells and assisted in scaling of the selection procedure to therapeutic cell numbers. Thus, these studies identified a strategy that requires only a brief ex vivo culture and does not use drug selection to obtain large numbers of functional gene-modified polyclonal T cells that can be used for adoptive immunotherapy.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Animals
  • Apoptosis / drug effects
  • CD28 Antigens / metabolism*
  • Cell Culture Techniques
  • Genes, T-Cell Receptor beta
  • Graft vs Host Disease / prevention & control
  • Humans
  • Immunomagnetic Separation* / methods*
  • Immunotherapy, Adoptive / methods*
  • Macaca
  • Receptor, Nerve Growth Factor / biosynthesis
  • Receptor, Nerve Growth Factor / genetics
  • Receptors, Lymphocyte Homing / metabolism
  • T-Lymphocytes / cytology
  • T-Lymphocytes / immunology
  • T-Lymphocytes / metabolism*
  • Thymidine Kinase / genetics
  • Thymidine Kinase / pharmacology
  • Transduction, Genetic / methods*

Substances

  • CD28 Antigens
  • Receptor, Nerve Growth Factor
  • Receptors, Lymphocyte Homing
  • Thymidine Kinase