Improved adenoviral vector for vascular gene therapy : beneficial effects on vascular function and inflammation

Circ Res. 2001 May 11;88(9):911-7. doi: 10.1161/hh0901.090926.

Abstract

First-generation, E1-deleted adenoviral vectors (E1-AV) can transduce the vascular endothelium with high efficiency, but their use is limited by the resulting acute endothelial injury and the long-term development of intimal hyperplasia. To reduce the impact of viral proteins on the gene-modified cells, a second-generation adenoviral vector with an additional pair of deletions in the E4 region was developed. To determine whether this E1/E4-AV vector would be useful for vascular gene transfer, we directly compared the efficiency of gene transfer to uninjured rabbit carotid arteries using either an E1/E4-AV or an E1-AV vector encoding beta-galactosidase. Both vectors efficiently transduced vascular endothelium; however, the E1/E4-AV vector gene-modified vessels showed higher beta-galactosidase expression 10 days after gene transfer. Importantly, the E1/E4-AV vector produced substantially less endothelial cell activation, less inflammation, and reduced neointimal hyperplasia compared with the E1-AV vector-treated vessels. The E1-AV vector-transduced vessels also demonstrated significantly impaired endothelium-dependent relaxation whereas the E1/E4-AV vector did not impact vasomotor function, even at doses of virus in 5-fold excess of the amount required for >90% transduction of the endothelium. We conclude that the E1/E4-AV vector is superior to the E1-AV vector for vascular gene therapy because of the prolonged transgene expression, reduced vascular inflammation, reduced intimal hyperplasia, and maintenance of normal vasomotor function.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenoviridae / genetics*
  • Adenovirus E1 Proteins / genetics
  • Adenovirus E1A Proteins / genetics
  • Adenovirus E4 Proteins / genetics
  • Animals
  • Carotid Arteries / metabolism
  • Carotid Arteries / pathology
  • Carotid Arteries / physiopathology
  • Endothelium, Vascular / metabolism
  • Endothelium, Vascular / physiopathology
  • Gene Expression Regulation
  • Genetic Therapy*
  • Genetic Vectors / genetics
  • Immunohistochemistry
  • Inflammation / genetics
  • Inflammation / therapy
  • Intercellular Adhesion Molecule-1 / metabolism
  • Male
  • Rabbits
  • Recombinant Fusion Proteins / genetics
  • Recombinant Fusion Proteins / metabolism
  • Transgenes / genetics
  • Tunica Intima / metabolism
  • Tunica Intima / pathology
  • Vascular Cell Adhesion Molecule-1 / metabolism
  • Vascular Diseases / genetics
  • Vascular Diseases / therapy*
  • Vasodilation / genetics
  • beta-Galactosidase / genetics
  • beta-Galactosidase / metabolism

Substances

  • Adenovirus E1 Proteins
  • Adenovirus E1A Proteins
  • Adenovirus E4 Proteins
  • Recombinant Fusion Proteins
  • Vascular Cell Adhesion Molecule-1
  • Intercellular Adhesion Molecule-1
  • beta-Galactosidase