Increased serum transferrin receptor concentrations in Friedreich ataxia

Ann Neurol. 2000 May;47(5):659-61.

Abstract

Mitochondrial iron accumulation is thought to underlie the pathophysiology of Friedreich ataxia and may occur at the expense of cytosolic iron. Decreases in cytosolic iron induce expression of the transferrin receptor, some of which is released into the serum. Here, we demonstrate that serum transferrin receptor concentrations are increased in patients with Friedreich ataxia, which supports the hypothesis that it is a disease of abnormal intracellular iron distribution.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Alleles
  • Child
  • Child, Preschool
  • Friedreich Ataxia / blood*
  • Friedreich Ataxia / genetics
  • Gene Expression / genetics
  • Humans
  • Point Mutation / genetics
  • RNA, Messenger / genetics
  • Receptors, Transferrin / blood*
  • Receptors, Transferrin / genetics
  • Severity of Illness Index
  • Trinucleotide Repeat Expansion / genetics

Substances

  • RNA, Messenger
  • Receptors, Transferrin